Rare disease

Peptides approved for small, specific conditions, often the first treatment of their kind.

5 peptides

  1. ApprovedElamipretideMitochondria-targeted cardiolipin-binding tetrapeptide4
  2. ApprovedVosoritideC-type natriuretic peptide (CNP) analogue39
  3. ApprovedAfamelanotideMelanocortin 1 receptor (MC1R) agonist13
  4. ApprovedSetmelanotideMelanocortin-4 receptor (MC4R) agonist8
  5. ApprovedTeduglutideGLP-2 analogue33

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  3. Approval
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