Rare disease
Peptides approved for small, specific conditions, often the first treatment of their kind.
5 peptides
- ApprovedElamipretideMitochondria-targeted cardiolipin-binding tetrapeptide4
- ApprovedVosoritideC-type natriuretic peptide (CNP) analogue39
- ApprovedAfamelanotideMelanocortin 1 receptor (MC1R) agonist13
- ApprovedSetmelanotideMelanocortin-4 receptor (MC4R) agonist8
- ApprovedTeduglutideGLP-2 analogue33